The aim of this questionnaire is to collect your insights on various aspects within the field of rare diseases (RDs). We begin with an overview of the current scenario and subsequently explore three distinct themes: value-based healthcare initiatives pertaining to rare diseases, early detection and neonatal screening practices, and the policies and regulatory procedures concerning rare diseases.
It will consist of 15 questions. The findings will be published in the upcoming issue of the International newsRARE magazine, scheduled for July 2024.
